Niemann-Pick Disease Type C - cyclotherapeutics

Cyclo Therapeutics, Inc. on X: #RareDisease clinical trials face different challenges than studies of larger patient populations. In @ClinicalLeader1 our CSO & SVP, #MedAffairs Sharon Hrynkow, Ph.D., shares learnings from our pivotal

About NPC - Firefly Fund

A new regulatory mechanism of STARD1 in Niemann-Pick disease type C (NPC), discovered

Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases

Therapeutic intervention for Niemann–Pick type C disease must target

PDF] Niemann-Pick Disease Type C in Adulthood - A Psychiatric and Neurological Disorder

Niemann-Pick disease type C, Orphanet Journal of Rare Diseases

Community News – NNPDF

Family Resources – NNPDF

Oxidative Stress: A Pathogenic Mechanism for Niemann-Pick Type C Disease

Niemann-Pick Type C Disease - Pipeline Insight, 2021

Cyclo Therapeutics, Inc. - Tonight at 7:30pm ET we're joining with the National Niemann-Pick Disease Foundation, Inc. as part of their Community Update webinar series to provide updates on TransportNPC, our pivotal