Niemann-Pick Disease, A Pipeline Analysis Report 2018

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a study of the pipeline molecules.

Niemann- Pick Disease Type C (NPC) Market Report 2023-2033 - Wissen Research

Global Niemann Pick Disease Type C Market to Surpass US$ 378.8 Million by 2027, Says Coherent Market Insights (CMI)

The GUaRDIAN framework. Clinicians refer patients and family members to

Magellan Rx Report - Spring 2023 by Magellan Rx Management - Issuu

An integrated multiomic approach as an excellent tool for the diagnosis of metabolic diseases: our first 3720 patients

Consensus clinical management guidelines for Niemann-Pick disease type C, Orphanet Journal of Rare Diseases

Frontiers Therapeutic Strategies For Tay-Sachs Disease

Biomolecules, Free Full-Text

PDF) Modeling Niemann–Pick disease type C in a human haploid cell line allows for patient variant characterization and clinical interpretation

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Estimated prevalence of Niemann–Pick type C disease in Quebec

Identification and Classification of Rare Variants in NPC1 and NPC2 in Quebec

Three-Dimensional Imaging of Whole-Body Zebrafish Revealed Lipid Disorders Associated with Niemann–Pick Disease Type C1