Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay

Human iPSC line TSD-01-hiPSC was generated from fibroblasts of a patient with infantile Tay-Sachs disease (TSD). The patient is compound heterozygous …

Presynaptic Dysfunction in Neurons Derived from Tay–Sachs iPSCs - ScienceDirect

Hexosaminidase a deficiency hi-res stock photography and images - Alamy

PDF) New Approaches to Tay-Sachs Disease Therapy

Frontiers Therapeutic Strategies For Tay-Sachs Disease

IJMS, Free Full-Text

Engineering of Human-Induced Pluripotent Stem Cells for Precise Disease Modeling

Frontiers The Linkage Phase of the Polymorphism KCNH2-K897T Influences the Electrophysiological Phenotype in hiPSC Models of LQT2

Biochemical Phenotype of GM1-iPSC-Derived Neural Stem Cells (A) b-GAL

Models to study basic and applied aspects of lysosomal storage disorders - ScienceDirect

Myelination and Node of Ranvier Formation in a Human Motoneuron–Schwann Cell Serum-Free Coculture

Role of induced pluripotent stem cells in lysosomal storage diseases - ScienceDirect

Frontiers New Approaches to Tay-Sachs Disease Therapy

PDF) Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay-Sachs disease patient

Intranasal Delivery of CRISPR-Cas9 Edited HEXA Gene to Treat Tay Sachs Disease in Newborn HEXA/NEU3-Deficient Mice — Le Pouls