5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

Niemann–Pick is a rare autosomal recessive inherited disease that is characterized by excessive accumulation of cholesterol and lipids in cells, leading to apoptosis and neural degeneration. The disease affects numerous body parts such as the brain, nerves, liver, spleen, bone marrow and lungs. Those suffering from the disease suffer from lack of coordination, dystonia; sleep disturbances, difficult in eating and swallowing and frequent bouts of pneumonia.

5 Most Promising Companies offering hope to patients with Niemann-Pick Type C

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Investigation of 2-Hydroxypropyl-β-Cyclodextrin Treatment in a Neuronal-Like Cell Model of Niemann–Pick Type C Using Quantitative Proteomics

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Australian NPC Disease Foundation Inc.

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And Life Goes OnAn Angel and a Rainbow: October 2017

Topic · Rare disease awareness ·

And Life Goes OnAn Angel and a Rainbow: October 2017

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